Longer-term Experience with Nusinersen in Teenagers and Young Adults with Spinal Muscular Atrophy: Results from the CS2/CS12 and SHINE Studies Day, J. W., Swoboda, K. J., Darras, B. T., Chiriboga, C. A., Iannaccone, S. T., De Vivo, D. C., Deconinck, N., Finkel, R. S., Tulinius, M., Saito, K., Montes, J., Sun, P., Bhan, I., Kandinov, B., Wong, J., Farwell, W. LIPPINCOTT WILLIAMS & WILKINS. 2020

View details for Web of Science ID 000536058002026