Onasemnogene Abeparvovec-xioi Gene-Replacement Therapy for Spinal Muscular Atrophy Type 1 (SMA1): Phase 3 US Study (STR1VE) Update Day, J. W., Chiriboga, C. A., Crawford, T. O., Darras, B. T., Finkel, R. S., Connolly, A. M., Iannaccone, S. T., Kuntz, N. L., Pena, L. M., Shieh, P. B., Smith, E. C., Schultz, M., Feltner, D. E., Tauscher-Wisniewski, S., Ogrinc, F. G., Shah, A., Ouyang, H., Macek, T., Kernbauer, E., Sproule, D. M., Mendell, J. R. LIPPINCOTT WILLIAMS & WILKINS. 2020

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