FIREFISH Part 1: 24-month safety and exploratory outcomes of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA) Baranello, G., Bloespflug-Tanguy, O., Darras, B., Day, J., Deconinck, N., Klein, A., Masson, R., Mercuri, E., Dodman, A., El-Khairi, M., Gerber, M., Gorni, K., Kletzl, H., Scalco, R., Servais, L. PERGAMON-ELSEVIER SCIENCE LTD. 2020: S122

View details for DOI 10.1016/j.nmd.2020.08.258

View details for Web of Science ID 000579727800251