Escalating dose and randomized, controlled study of high-dose nusinersen in SMA; study design and updated enrollment for the DEVOTE Study Finkel, R., Day, J., Ryan, M., Mercuri, E., De Vivo, D., Pascual, S., Montes, J., Gurgel-Giannetti, J., Mitchell-Sweeney, N., Foster, R., Sun, P., Ramirez-Schrempp, D., Kandinov, B., Farwell, W. PERGAMON-ELSEVIER SCIENCE LTD. 2020: S124

View details for DOI 10.1016/j.nmd.2020.08.264

View details for Web of Science ID 000579727800257