One-time administration of AVXS-101 intrathecal (IT) for spinal muscular atrophy in the phase 1 study (STRONG): safety report Chand, D., Finkel, R., Day, J., Darris, B., Kuntz, N., Connolly, A., Zaidman, C., Crawford, T., Butterfield, R., Shieh, P., Tennekoon, G., Brandesma, J., Iannaccone, S., Meriggioli, M., Tauscher-Wisniewski, S., Shoffner, J., Ogrinc, F., Kavanagh, S., Feltner, D., Mendell, J. PERGAMON-ELSEVIER SCIENCE LTD. 2020: S120

View details for DOI 10.1016/j.nmd.2020.08.254

View details for Web of Science ID 000579727800247