Escalating Dose and Randomized, Controlled Study of Nusinersen in Participants With Spinal Muscular Atrophy (SMA); Study Design and Part A Data for the Phase 2/3 DEVOTE (232SM203) Study to Explore High Dose Nusinersen Day, J. W., Pascual, S., Finkel, R. S., Ryan, M. M., Mercuri, E., De Vivo, D. C., Montes, J., Gurgel-Giannetti, J., Gambino, G., Nuzzo, R., Makepeace, C., Berger, Z. LIPPINCOTT WILLIAMS & WILKINS. 2021

View details for Web of Science ID 000729283602113