SUNFISH 3-YEAR EFFICACY AND SAFETY OF RISDIPLAM IN TYPES 2 AND 3 SMA Servais, L., Day, J. W., Mazzone, E. S., Oskoui, M., Baranello, G., Gerber, M., Martin, C., McIver, T., Yeung, W., Mercuri, E. BMJ PUBLISHING GROUP. 2022

View details for DOI 10.1136/jnnp-2022-abn2.232

View details for Web of Science ID 000841239400136