A phase 1/2 clinical trial evaluating the safety and pharmacokinetics of AOC 1001 in adults with myotonic dystrophy type 1: MARINA study design Johnson, N., Day, J., Hamel, J., Statland, J., Subramony, S., Arnold, W., Thornton, C., Wicklund, M., Soltanzadeh, P., Knisely, B., Goel, V., DiTrapani, K., Chen, C., Clark, K., Peters, A., Heusner, C., Younis, H., Tai, L., Ackermann, E. PERGAMON-ELSEVIER SCIENCE LTD. 2022: S131

View details for DOI 10.1016/j.nmd.2022.07.372

View details for Web of Science ID 000873062200365