SUNFISH Parts 1 and 2: 4-year Efficacy and Safety Data of Risdiplam in Types 2 and 3 Spinal Muscular Atrophy (SMA) Servais, L., Oskoui, M., Day, J., Deconinck, N., Mazzone, E., Nascimento, A., Saito, K., Vuillerot, C., Baranello, G., Boespflug-Tanguy, O., Goemans, N., Kirschner, J., Kostera-Pruszczyk, A., Braid, J., Papp, G., Gorni, K., Martin, C., Scalco, R., Yeung, W., Mercuri, E. LIPPINCOTT WILLIAMS & WILKINS. 2023

View details for DOI 10.1212/WNL.0000000000203570

View details for Web of Science ID 001053672107199