Preliminary Assessment of the Phase 1/2 Clinical Trial Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Patients with Myotonic Dystrophy Type 1 (DM1) (MARINA) Johnson, N., Day, J., Hamel, J., Thornton, C., Subramony, S., Soltanzadeh, P., Statland, J., Arnold, W., Wicklund, M., Ditrapani, K., Heusner, C., Chen, C., McEvoy, B., Zhu, Y., Tai, L., Ackermann, E. LIPPINCOTT WILLIAMS & WILKINS. 2023

View details for DOI 10.1212/WNL.0000000000202529

View details for Web of Science ID 001053672108045