COMET: Patient-reported outcome measures in patients with late-onset Pompe disease after 145 weeks' avalglucosidase alfa Toscano, A., Kishnani, P., Diaz-Manera, J., Kushlaf, H., Ladha, S., Mozaffar, T., Straub, V., Van der Ploeg, A., Clemens, P., Day, J., Illarioshkin, S., Roberts, M., Attarian, S., Carvalho, G., Erdem-Ozdamar, S., Goker-Alpan, O., Kostera-Pruszczyk, A., Haack, K., Huynh-Ba, O., Tammireddy, S., Thibault, N., Zhou, T., Dimachkie, M., Schoser, B., Comet Invest Grp WILEY. 2023: 209-210

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