Safety update: Risdiplam clinical trial program for spinal muscular atrophy (SMA) Baranello, G., Chiriboga, C., Servais, L., Darras, B., Day, J., Deconinck, N., Farrar, M., Finkel, R., Bertini, E., Kirschner, J., Rasson, M., Mazurkiewicz-Beldzinska, M., Vlodavets, D., Bader-Weder, S., Gorni, K., Jaber, B., Yeung, W., Papp, G., Scalco, R., Mercuri, E., FIREFISH SUNFISH JEWELFISH RAINBOW PERGAMON-ELSEVIER SCIENCE LTD. 2023: S92-S93

View details for DOI 10.1016/j.nmd.2023.07.112

View details for Web of Science ID 001087070800102