Topline safety and efficacy data analysis of phase 1/2 clinical trial evaluating AOC 1001 in adults with myotonic dystrophy type 1: MARINA ™ Johnson, N., Day, J., Hamel, J., Thornton, C., Subramony, S., Soltanzadeh, P., Statland, J., Wicklund, M., Arnold, W., Freimer, M., DiTrapani, K., Heusner, C., Chen, C., McEvoy, B., Zhu, Y., Tai, L., Ackermann, E. PERGAMON-ELSEVIER SCIENCE LTD. 2023: S190-S191

View details for DOI 10.1016/j.nmd.2023.07.487

View details for Web of Science ID 001087070800476