Sunfish parts 1 and 2: 4-year efficacy and safety data of risdiplam in types 2 and 3 spinal muscular atrophy (SMA) Oskoui, M., Deconinck, N., Mazzone, E. S., Nascimento, A., Day, J. W., Saito, K., Vuillerot, C., Baranello, G., Boespflug-Tanguy, O., Goemans, N., Kirschnero, J., Kostera-Pruszczyk, A., Servais, L., Braid, J., Gerber, M., Gorni, K., Martin, C., Yeung, W., Scalco, R. S., Mercuri, E. ELSEVIER. 2023

View details for DOI 10.1016/j.jns.2023.121096

View details for Web of Science ID 001163199100226